A Brand New Network for
Gene Therapy Success

Built by Gene Therapy experts for Gene Therapy experts focused on the treatment of rare disorders

This network’s mission is to accelerate the delivery of safe, efficacious and accessible gene therapies to rare disease patients faster

Its purpose is to assemble unique experience-sharing collectives of gene therapy specialists to work together to tackle their most pressing shared clinical, manufacturing and regulatory challenges

It is the only global gene therapy network focused on rare disorders that allows the whole team to engage in the timely,  targeted exchanges of experiences and ideas in mission-critical pre-competitive areas

Make better informed GTx development decisions

Adopt new clinical, manufacturing and regulatory approaches through regular exchange of experiences and access to a unique shared resource hub

Plug into a ready-made
expert network

Save time and money by accessing a dedicated network of peers you can engage without having to travel via a member-only gene therapy directory

Influence the development of new industry standards

Collaborate and act as a singular voice to influence regulators and set industry standards, through an annual white paper and community position paper

Members are gene therapy specialists focused on rare disorders including:

Searchlight - LEAP HR - Exec Summary lock up (6)

Membership brochure

For more information on what is included as part of the Gene Therapy for Rare Disorders: Searchlight membership please download our membership brochure.

What will you learn? 

  • What's included in membership 
  • The member experiences 
  • The benefits of membership 
  • Who can you expect to be networking with? 
  • How to join the network

Our members say it best...

Tayler Renshaw, Head of Regulatory Affairs CMC, Astellas Gene Therapies

“Many of the working groups that are already out there are so similar, but this is different because it’s so focusedstructured and value-driven, which makes it a need-to-attend, not a nice-to attend, which is why we are taking part.”

Adam Silverman, Director of Therapeutics Discovery, Codexis

“We’ve all got internal expertise, but we need more external perspective. There’s so much value to be gained from a facilitated, structured network like this because it focuses sharing the lessons learned from failures as well as successes.”

Nicole Paulk, AAV Gene Therapy Thought Leader, University of San Francisco

“We’re all facing the same road blocks, so we need a new way to get past the hurdles that are slowing us down. The fact that everyone’s showing up to this network looking to actively add value is it’s secret weapon.”

To read more reviews about Gene Therapy for Rare Disorders: Searchlight membership, visit our testimonials page. 

Who qualifies for the Gene Therapy for Rare Disorders Searchlight network?


Strategic GTx-focused leaders

Member companies are represented by one internal champion who has strategic oversight over its gene therapy program

Motivated to share

Members will require a collaborative mindset, focused on what can be shared rather than being defined by what can’t

In sight of the clinic

Members will be curated based on development stage (with those either in or close to reaching the clinic having priority)