A Brand New Network for Gene
Therapy Success

A global network of drug developers united in accelerating the delivery of safe,
efficacious and accessible gene therapies to rare disease patients

A private network for gene therapy drug developers

designed by gene therapy drug developers

2022 was a landmark year for the global gene therapy space. Last August came the green light for bluebird bio’s Zynteglo in the US, the first FDA approval for a gene therapy in over three years. Hot off its heels, we saw the accelerated approval of another bluebird bio product, Skysona.

As the gene therapy field continues to break records, there are still significant challenges to overcome relating to safety, efficacy, and accessibility.

For this reason, your peers from some of the most innovative pharma and biotech companies have designed the  Gene Therapy for Rare Disorders Searchlight  network to accelerate the safe delivery of gene therapies to rare disorder patients.

Its purpose is to assemble unique experience-sharing collectives of gene therapy specialists to work together to tackle their most pressing shared clinical, manufacturing and regulatory challenges

It is the only global gene therapy network focused on rare disorders that allows the whole team to engage in the timely,  targeted exchanges of experiences and ideas in mission-critical pre-competitive areas.

Join your peers today and be part of a global community of like-minded individuals:

GTx Searchlight - Getting more insights on regulatory experiences, expectations and any changes in the rules
GTx Searchlight - What expectations are around clinical safety – what the focus needs to be and how this influences decision-making
GTx Searchlight - How to predict, monitor and mitigate against immunogenicity

Business critical conversations

Virtual cornerstone meetings

We facilitate, structured, discussion-driven, Gene Therapy-focused quarterly meetings for member companies.

Each high-impact 90-minute meeting takes place virtually via Zoom. The meeting agenda is carefully curated and focused on the topics and critical challenges requested by Searchlight members.

Member companies are represented by one internal champion with strategic oversight over its Gene Therapy program to ensure that each discussion is high-value, high-impact, and delivers tangible outputs for members to take back to their organization.

Innovation doesn't happen in isolation

Searchlight makes meaningful progress

Astellas Gene Therapy“Many of the working groups that are already out there are so similar, but this is different because it’s so focused, structured and value-driven, which makes it a need-to-attend, not a nice-to attend, which is why we are taking part.”

“We’ve all got internal expertise, but we need more external perspective. There’s so much value to be gained from a facilitated, structured network like this because it focuses sharing the lessons learned from failures as well as successes.”

“There’s more accepted practice that isn’t documented in GTx than anywhere else. If you need specific information about the art, you need to know someone who has the answer. This network will help us find the answers we need faster.”

The Searchlight platform

Network with the best in the field

Gain insider knowledge and insights from scientific advisors

David Dobnik Senior Research Associate_National Institute of Biology  

David Dobnik
 Senior Research Associate
National Institute of Biology

Nicole Paulk Professor UCSF

Nicole Paulk

Searchlight - LEAP HR - Exec Summary lock up (6)

Membership brochure

For more information on what’s included as part of the Gene Therapy for Rare Disorders: Searchlight membership, please download the membership brochure. 

Here’s what you’ll learn more about: 

  • The unique mission and purpose of the network 
  • What membership includes 
  • How the quarterly cornerstone meetings work 
  • How bespoke value delivery works 
  • How we deliver demonstrable value to you 
  • Annual member investment 

The Searchlight platform

Build meaningful relationships and gain value all year around

GTX Searchlight - App animation - (400 × 400 px)

Instant messaging

Contact fellow members via the private or group chat features.

Member meetups

Come together with leaders throughout the community at virtual cornerstone meetings and in-person gatherings at Hanson Wade conferences.

On demand

Explore the library of business critical content and videos on demand via the thematic rooms and content channels.

Apply today to join the GTx network

Tap into a ready-made collaborative working group to solve common challenges together